The research is focused on identifying biomarkers, non-ambulatory endpoints in duchenne muscular dystrophy.
Funds will allow recruitment of 100 additional subjects and expand the study through the 20 Cooperative International Neuromuscular Research Group centers to understand the disease advancement and conclude the impact of the Centers for Disease Control established Duchenne standards of care.
The UC Davis physical medicine and rehabilitation department professor and chair McDonald said PPMD funding will aid in the development of new outcome measures and the overall quality of the data.
"These studies have already impacted the development of endpoints for trials in Duchenne and the new funding will allow us to extend the research into younger boys and boys who have not yet started taking steroids," McDonald added.