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Amicus is developing the investigational pharmacological chaperone Migalastat HCl under collaboration with GlaxoSmithKline. Study 012, designed to compare oral migalastat HCl to ERTs (Fabrazyme and Replagal), enrolled Fabry

CTP-499 is a potential treatment developed on the basis of DCE Platform for diabetic nephropathy, a form of chronic kidney disease. The composition of matter and pharmaceutical compositions

Alnylam’s ALN-TTR program includes ALN-TTR02 and ALN-TTRsc, a subcutaneously administered RNAi therapeutic. Alnylam chief executive officer John Maraganore said ALN-TTR program holds promise as a breakthrough therapy for

The EMA’s opinion if ratified by European Commission will enable Krystexxa to treat tophaceous gout patients, who have failed to normalise serum uric acid with xanthine oxidase inhibitors

Under the new pathway, the FDA is expected to allow developers of such drugs to conduct smaller, faster clinical trials and provide a "special medical use" label enabling

Activ-Blister desiccant film technology monitors the internal atmosphere of each individual blister cavity to safe guard moisture- and oxygen-sensitive solid-dose pharmaceuticals leading to product stability, increased shelf life

The new facility will utilize 100% disposable equipment for manufacturing biologics drug substances. WuXi AppTec chairman and CEO Ge Li said the establishment of the cGMP biologics facility

The tablet, which is the AB-rated generic equivalent of Nordette, is a  Levonorgestrel and Ethinyl estradiol combined oral contraceptive used to prevent pregnancy. Kurvelo tablets are being marketed

The recommendation requires to be ratified by decision of the European Commission which is expected within the next 74-90 days and if approved Betmigatm will be a new