Santhera receives EMA acceptance for idebenone MAA review
The MAA submission was based on the RHODOS study results which was, a placebo-controlled, randomized trial and has demonstrated efficacy of idebenone in LHON. The MAA also includes
miRecule has signed a research collaboration with EM subsidiary Rio Biofarma Brasil (RBBL) to co-develop peptide-mediated delivery technologies aimed at improving targeted ribonucleic acid (RNA) therapeutics delivery to tissues beyond the liver and muscles in a range of disease areas.