Sobi’s metabolic disorder drug secures fast track status in US
MPS IIIA, a rare metabolic disorder also known as Sanfilippo syndrome type A, affects children from an early age. The condition results in severe deterioration of the central nervous
miRecule has signed a research collaboration with EM subsidiary Rio Biofarma Brasil (RBBL) to co-develop peptide-mediated delivery technologies aimed at improving targeted ribonucleic acid (RNA) therapeutics delivery to tissues beyond the liver and muscles in a range of disease areas.
SymBio holds approval for TREAKISYM injectables which are already used for the treatment of three indications of malignant lymphoma (first-line and relapsed/refractory low-grade B-cell non-Hodgkin's lymphoma and mantle