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The first-in-man clinical trial utilizes a single intravenous injection of AAV gene therapy for patients with MPS IIIA (Sanfilippo syndrome type A), a devastating lysosomal storage disease that

This study, which will enroll 40 healthy adults in U.S. sites, follows a successful Phase 1a single ascending dose clinical study completed in 2016. Preclinical studies have shown

The IND is now active and Audentes plans to initiate VALENS, the multicenter, multinational, open-label, ascending dose phase 1 / 2 clinical study of AT342. Preliminary data from

Xyzal is a single daily dose oral antihistamine, with an active ingredient of levocetirizine dihydrochloride that relieves runny nose, sneezing, itchy watery eyes and itching of the nose

The assets acquired have been developed by Cantab Anti Infectives Ltd, a PBB group company. Ankit Mahadevia, M.D., Chief Executive Officer of Spero, said: “The acquisition of these

Scientists are searching for chemical drug candidates that can affect the key molecules and proteins that control cancer cells in several common childhood cancers. However, finding drug candidates

REVIVE-1 is a 600-patient double-blinded, global, multicenter trial, in patients with ABSSSI that compares the safety and efficacy of an 80mg intravenous dose of iclaprim with 15mg/kg intravenous

The project builds on work at the university to understand the role apelin receptors play in cardiovascular diseases. The collaboration gives Heptares access to a group run by Anthony Davenport,

The drug is approved as the first adjunctive therapy in the European Union (EU) for patients aged two years and older. The EC’s decision marks the third TSC-related