FDA grants orphan drug status for Arrowhead’s ARC-AAT to treat liver disease
AATD is a rare genetic disease that severely damages the liver and lungs of affected children and adults. Currently, the company is conducting part B of a Phase
Tolerance Bio has signed an agreement securing an exclusive licence from Tanabe Pharma for TLB-33, a clinical-stage anti-IL-33 monoclonal antibody, in a deal that includes potential development and sales milestone payments of up to around $560m.
Based on achieving this critical milestone, Aspyrian Therapeutics recently submitted and has received FDA’s acceptance of an Investigational New Drug (IND) Application for RM-1929, their first-in-class, precision targeted