Vertex Pharmaceuticals' Kalydeco (ivacaftor, VX-770) drug, that targets the defective protein responsible for cystic fibrosis (CF) showed efficacy in Phase 3 trial.
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The data was published in the New England Journal of Medicine (NEJM).
The Phase 3 STRIVE study evaluated 161 patients 12 years or older who received at least one dose of either Kalydeco as a single 150 mg tablet or placebo twice daily.
The data demonstrated improvements in lung function and other measures of disease throughout the 48week study.
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